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Eplontersen approved to treat adults with rare inherited nerve disease or polyneuropathy

Home / United Kingdom / Eplontersen approved to treat adults with rare inherited nerve disease or polyneuropathy
Eplontersen approved to treat adults with rare inherited nerve disease or polyneuropathy
  • April 5, 2025
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Eplontersen approved to treat adults with rare inherited nerve disease or polyneuropathy

The Medicines and Healthcare products Regulatory Agency (MHRA) has approved eplontersen (Wainzua) to treat adults with polyneuropathy associated with hereditary transthyretin amyloidosis (ATTRv), which is a rare progressive …

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